Gene Therapy Curing X-Linked Retinitis Pigmentosa in Dogs Paves the Way for Similar Treatment in Humans
March 19, 2012
Researchers at several universities and laboratories collaborated to treat dogs afflicted with the x-linked form of retinitis pigmentosa, to deliver the therapeutic RPGR gene specifically to the diseased rods and cones. This led to functional and structural recovery, and is the first proof that this condition is treatable in an animal model. The researchers concluded that the results are promising and relevant for translation to humans afflicted with this disease.
The results have been published in the journal, Proceedings of the National Academy of Sciences.
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